Guri-Lamce, Ina;
Alrokh, Yara;
Graham, Carina;
Maeshima, Ruhina;
Rognoni, Emanuel;
Caley, Matthew;
Łaczmański, Łukasz;
... Jacków-Malinowska, Joanna; + view all
(2024)
Lipid Nanoparticles Efficiently Deliver the Base Editor ABE8e for COL7A1 Correction in Dystrophic Epidermolysis Bullosa Fibroblasts In Vitro.
Journal of Investigative Dermatology
10.1016/j.jid.2024.03.027.
(In press).
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| Type: | Article |
|---|---|
| Title: | Lipid Nanoparticles Efficiently Deliver the Base Editor ABE8e for COL7A1 Correction in Dystrophic Epidermolysis Bullosa Fibroblasts In Vitro |
| Location: | United States |
| Open access status: | An open access version is available from UCL Discovery |
| DOI: | 10.1016/j.jid.2024.03.027 |
| Publisher version: | http://dx.doi.org/10.1016/j.jid.2024.03.027 |
| Language: | English |
| Additional information: | ©2024 The Authors. Published by Elsevier, Inc. on behalf of the Society for Investigative Dermatology. This is an open access article under the CC BY license (http://creativecommons.org/licenses/by/4.0/). |
| Keywords: | Epidermolysis bullosa, Gene editing, Gene therapy, Lipid nanoparticles |
| UCL classification: | UCL UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Population Health Sciences > UCL GOS Institute of Child Health UCL > Provost and Vice Provost Offices > School of Life and Medical Sciences > Faculty of Population Health Sciences > UCL GOS Institute of Child Health > Genetics and Genomic Medicine Dept |
| URI: | https://discovery-pp.ucl.ac.uk/id/eprint/10191387 |
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