Farag, Mena;
Tabrizi, Sarah J;
Wild, Edward J;
(2024)
Huntington’s Disease Clinical Trials Update: September 2024.
Journal of Huntington's Disease
, 13
(4)
pp. 409-418.
10.1177/18796397241293955.
Preview |
Text
Farag_Ms. No. JHD-240072 - Accepted.pdf Download (463kB) | Preview |
Abstract
In this edition of the Huntington's Disease Clinical Trials Update, we expand on the ongoing extension study of PTC518 from PTC Therapeutics, including 12-month interim results from the parent study. We also discuss 24-month interim results from uniQure's AMT-130 program and 28-week follow-up results from Wave Life Sciences’ SELECT-HD clinical trial of WVE-003. Additionally, we provide a comprehensive listing of all currently registered and ongoing clinical trials in Huntington's disease.
Archive Staff Only
![]() |
View Item |